Search references for DFT383. Phrases containing DFT383
See searches and references containing DFT383!DFT383
Investigational gene therapy
DFT383 is an investigational gene therapy under development by Novartis for the treatment of cystinosis, a rare autosomal recessive lysosomal storage disorder
DFT383
Lysosomal storage disease
thereby reducing cystine accumulation in various tissues. AVR-RD-04 (now DFT383 by Novartis) This investigational gene therapy, initially developed by AVROBIO
Cystinosis
DFT383
DFT383
DFT383
DFT383
Biblical
bitter contrition, without judgment
Boy/Male
Arabic, Muslim
Silent
Boy/Male
Hindu
Girl/Female
Hindu, Indian, Telugu
Strength of Mind; Prayer; Love
Female
Italian
Italian and Spanish form of Latin Elwisia, ELOISA means "hale-wide; very healthy and sound."Â
Boy/Male
Hindu
Great one
Boy/Male
Hindu, Indian
Son of Lord Varun
Girl/Female
Hindu, Indian, Kannada, Marathi, Sindhi, Tamil, Telugu, Thai, Traditional
Meditation
Boy/Male
Native American
Porcupine bear.
Boy/Male
Arabic, Muslim
Skilful
DFT383
DFT383
DFT383
DFT383
DFT383